US FDA approves Zevra's treatment for rare genetic disease
The U.S. Food and Drug Administration has approved Zevra Therapeutics' drug for a rare and fatal genetic disorder, making it ...
Psychology Today1d
How I Survived a Rare Autoimmune Disease
I walked out of my marriage and immediately fell ill. I was ill for two years. At first, I thought it was a cold that would ...
Health officials in L.A. Co. investigating rare disease spread from raccoons to humans
The Los Angeles County Department of Public Health is looking into two human cases of a rare parasitic infection that comes ...
‘Survivor 47’ preview: Terran ‘TK’ Foster on facing death’s door because of ‘pretty rare kidney disease’ [WATCH]
Survivor 47” fans, it’s time to meet Terran “TK” Foster, a 31-year-old athlete marketing manager from Upper Marlboro, ...
'One small step': Community comes together for Swansea 1-year-old with rare liver disease
A walk-a-thon fundraiser steps off in New Bedford this weekend in support of "Saige the Brave" following the 1-year-old's ...
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FDA approves first drug for rare neuron disease, Niemann-Pick type C
The Food and Drug Administration on Friday approved the first treatment for Niemann-Pick disease, type C, the culmination of ...
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House panel passes pediatric rare disease bill, setting it up for government funding bill
A House committee on Wednesday passed a bill to renew a program aimed at aiding development of drugs for rare diseases in ...
FierceBiotech2d
FDA scraps adcomm for Applied's rare disease drug ahead of November decision
After pushing back the decision date for Applied Therapeutics’ metabolic disorder drug govorestat, the FDA has now decided ...
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Calves to Cure helps fund research for Worden boy's rare disease
The Billings Livestock Commission hosted the sixth annual Calves to Cure on Thursday, an event to help raise money and ...
KTVQ Billings, MT on MSN15h
Calves to Cure helps fund research for rare disease battled by Worden boy
This U.S. Army film tells the story of a Japanese woman who marries an American serviceman and goes with him to the United ...
FDA Approves Zevra's Miplyffa for Niemann-Pick Disease Type C -- 2nd Update
Zevra Therapeutics has won Food and Drug Administration approval of Miplyffa for Niemann-Pick disease type C, or NPC, making it the first drug cleared in the U.S. for the rare neurodegenerative ...