PTC’s strong third quarter and breakout Sephience launch may help explain why one life-sciences fund is quietly upping its ...
A new AI model called popEVE can predict how likely each variant in a patient’s genome is to cause disease. The team is ...
An experimental vaccine has saved lives in an early clinical trial for a rare form of liver cancer that primarily affects younger patients, researchers with Johns Hopkins Kimmel Cancer Center ...
Regeneron is adding its name to Tessera Therapeutics’ unique in vivo gene writing program, inking a deal that lets it in on a ...
The multi-year partnership launches with focus on epilepsy, rare disease and AISAN FRANCISCO and ATLANTA, Dec. 02, 2025 ...
8don MSN
California boy, 3, receives first-ever gene therapy for his rare disease: ‘It’s just so exciting’
A California toddler is the first person in the world to receive gene therapy to treat his devastating disease.
Rare disease research faces complex regulations, small patient populations, and high costs. As traditional incentives wane, ...
A 9-year-old Midlands student made his return to school Tuesday after finishing treatment for a rare genetic disorder.
The U.S. House of Representatives has given a unanimous thumbs up to the Give Kids A Chance Act, which would revive the FDA’s rare pediatric review voucher program following its expiration in December ...
In 2024, Washoe County saw a nearly 38% increase in reported Lyme disease cases from the previous year, from eight cases to ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback